The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

The UK has approximately 17,500 individuals living with sickle cell disease, a condition particularly prevalent amongst those ...

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

Discover the importance of vision, genetic eye disorders, and RNA-based therapies for precision treatment in India and ...

There are 20 cell and gene therapies on Europe's market versus 43 in the U.S. Find out more about this ecosystem.

These symbiotic relationships provide clues as to how genetic material was exchanged ... to digest plant cell wall components. For example, pectinases are enzymes that break down pectins ...

Even though a large proportion of cancer patients carry genetic mutations that make them more susceptible to cancer, only a small percentage of them — and their family members — undergo ...

Gene therapy has been available since 2022 for hemophilia B and since 2023 for hemophilia A, yet some major medical institutions have barely treated any patients so far. What’s the holdup?

For 30 years, researchers have known that Huntington’s disease is caused by an inherited mutation in the Huntingtin (HTT) gene in which a three-letter ... involved in maintaining and repairing DNA.

It may be, she added, that weekly therapy sessions are simply not scalable to a broad population, and the field should explore light-touch alternatives, like single-session interventions and ...

The company is advancing its Phase I/II trial and exploring accelerated approval pathways in the US and Europe.

Scientists have found 697 genetic variants – or small changes within a gene – linked to depression, of which almost 300 were previously unknown. A Queensland scientist described the project as ...