The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

Discover the importance of vision, genetic eye disorders, and RNA-based therapies for precision treatment in India and ...

There are 20 cell and gene therapies on Europe's market versus 43 in the U.S. Find out more about this ecosystem.

The UK has approximately 17,500 individuals living with sickle cell disease, a condition particularly prevalent amongst those ...

Invest in SPDR S&P Biotech ETF (XBI) for long-term growth potential and diverse, equal-weighted portfolio in the biotech ...

The HDBuzz team caught up with editor emeritus and Huntington's disease specialist, Prof Ed Wild to hear his thoughts on what ...

President Trump signed an executive order on the day of his inauguration that created doubts about the future of a program to ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and bone marrow transplantation—to alleviate symptoms of multiple ...

Sidra Medicine, a member of Qatar Foundation, has established a Gene Therapy Center to treat rare genetic diseases such as Spinal Muscular Atrophy (SMA) and Duchenne Muscular Dystrophy (DMD). The ...

A team of investigators from Dana-Farber Cancer Institute, The Broad Institute of MIT and Harvard, Google, and Columbia University have created an artificial intelligence model that can predict which ...