Sangamo reports updated data for gene therapy candidate ST-920
Sangamo (SGMO) reported positive updated data from a Phase 1/2 study of its gene therapy candidate ST-920 in the treatment of Fabry disease. Read more here.
Nanomachines loaded with wine ingredients overcome gene therapy challenges
Researchers have demonstrated, for the first time in the world using mice, the ability to overcome significant challenges in ...
Tenaya Therapeutics Receives $8 Million Clinical Grant from California Institute for Regenerative Medicine
Tenaya Therapeutics, Inc. (NASDAQ: TNYA), a clinical-stage biotechnology company with a mission to discover, develop and deliver potentially curative therapies that address the underlying causes of ...
Gene therapy and bone marrow transplant alleviate ultra-rare genetic disease symptoms
In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and ...
BioSpace11d
Duchenne Muscular Dystrophy Space on Cusp of Pivotal Era
While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...
pharmaphorum15d
Pfizer agrees $630m deal to harness Voyager's gene therapy tech
Pfizer is paying Voyager $30 million upfront to get access to its TRACER adeno-associated virus (AAV) vector technology ... its VY-HTT01 gene therapy for Huntington disease on clinical hold ...
Yahoo! Sports15d
How Rensselaer football RB used heart, family to become top small-school offensive player
The senior captain used his size as an advantage, recalling how he was one of the smallest players on the Rensselaer Pop Warner team at 5 years old.
verywellhealth15d
Heart Disease
Heart disease is a term used to describe a constellation of conditions that can affect the heart and/or its valves, vessels, structure, electrical system, or coronary arteries. Though each disease ...
Medscape23d
Gene Therapy in Hemophilia: High Hopes and Costs, Low Uptake
Patients must have serious disease ... Why can’t patients get gene therapy more than once? Because patients can develop immunity to the viral vector used to deliver the therapy.
IEEE23d
Cooperative Path Planning of Multiple Unmanned Aerial Vehicles Using Cylinder Vector Particle Swarm Optimization with Gene Targeting
Therefore, a novel cylindrical coordinate particle swarm optimization (PSO) planner with gene targeting (GTCPSO) is presented to obtain feasible and accurate flight routes for multiple UAVs. In GTCPSO ...
GEN24d
JPM: Roche Licenses Dyno Therapeutics’ AAV Vector for Neurological Gene Therapy
Dyno Therapeutics announced that Roche has exercised its option to license a novel capsid for use in a gene therapy program for an undisclosed neurological disease. The capsid license follows an ...
News Medical24d
New gene-editing treatment extends lifespan in mice with prion disease
Researchers at the Broad Institute of MIT and Harvard have developed a gene-editing treatment ... against the disease. "We realized it was this golden opportunity to use human genetics to inform ...