Zandy Forbes’ biotech company MeiraGTx has developed targeted gene therapy methods to treat more than just genetic disorders.

Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

Financially, Monopar has a cash runway until 2026 but will need additional funds for commercialization efforts. See why I'm ...

COPA syndrome causes lung hemorrhaging starting in childhood. But one in three people with the disease mutation are spared.

Ten of 11 children born with a rare form of congenital hearing loss experienced improvements after receiving the company’s ...

The pioneering gene therapy developer will be acquired by investment firms Carlyle Group and SK Capital for a fraction of ...

Gene therapy for another form of genetic blindness ... each - a measure taken in case the treatment had any adverse effects. They were aged between one and three when they had the procedure ...

ElevateBio is seeking out partnerships for its lead gene therapy after the construct reduced the levels of a toxic protein in ...