Australian cancer researchers are the first to establish a next-generation gene-editing tool for modeling and interrogating human disease.

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...

The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...

Around 1,700 people could be eligible for the one-time treatment, which is seen as a less risky alternative to a donor stem ...

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...

A GROUNDBREAKING genetic treatment with the potential to cure sickle cell disease will be rolled out on the NHS. The one-off ...

Discover the importance of vision, genetic eye disorders, and RNA-based therapies for precision treatment in India and ...

Intranasal foralumab can modulate a number of immune cell types in people with non-active SPMS, developer Tiziana Life ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and ...

However, significant barriers stand in the way of realising this promise on a worldwide scale, from manufacturing costs and ...

Scientists have discovered a potential new treatment for familial hypercholesterolemia, inspired by signs seen in the Mona ...