In February 2024, when she was five, Liliana was diagnosed with Morquio syndrome — also known as mucopolysaccharidosis type ...

For the first time, Hospital Kuala Lumpur (HKL) is proudly hosting the annual Rare Disease Day 2025 celebration to raise ...

Detailed price information for Biomarin Pharmaceuticals (BMRN-Q) from The Globe and Mail including charting and trades.

The enzyme replacement therapy (ERT) market is projected to grow significantly, rising from US$ 10,707.6 million in 2024 to US$ 20,289.1 million by 2034, at a robust CAGR of 6.60% over the forecast ...

Moroquio Syndrome, sila po ay mga storage disorder, and Osteogenesis Imperfecta or little bone Disease,” she said. She stressed that “together we can bring awareness to diseases, stories and ...

Rare diseases are individually rare, affecting <5 in 10,000 people worldwide, yet collectively common, affecting 6%−8% of the human population (Dawkins et al., 2018). An estimated 6,000–8,000 disease ...