The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...

The gene-editing treatment will be available to certain patients with sickle cell disease in England as Vertex commits to collecting additional data.

Billie Eilish and Green Day kicked off the FireAid benefit concert in Los Angeles on Thursday night - a two-venue, five-hour ...

President Trump signed an executive order on the day of his inauguration that created doubts about the future of a program to ...

REGENXBIO is a longtime player in the gene therapy space, but one that’s yet to bring its own therapy to market (in the early ...

Fractyl Health is deprioritizing a type 2 diabetes trial in favor of a pivotal study of its endoscopy treatment Revita and ...

In the latest development, the European Commission has asked the EMA's human medicines committee, the CHMP, to take a look at ...

Kadimastem’s attempt to vault onto Nasdaq is picking up momentum, with shareholders signing off on a merger with NLS Pharmaceutics that would enable the cell therapy developer to recover from last ...

The Exa-cel gene therapy treatment is at the forefront of medical technology. It takes the person’s DNA and “edits” out the faulty sickle gene. It’s expensive, too. According to the manufacturer, ...

NHS officials estimate around 50 people a year will receive treatment now it has been approved for use for certain patients with severe sickle cell disease. | ITV National News ...

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...