The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

Despite mixed results using gene therapies to treat Duchenne muscular dystrophy, drug developers are pushing ahead with the ...

President Trump signed an executive order on the day of his inauguration that created doubts about the future of a program to ...

CDMO Rentschler Biopharma is signalling its intent to cut down cell and gene therapy operations by shutting down its UK ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and ...

The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...

People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...

This new tool, known as minimal, versatile genetic perturbation technology (mvGPT), combines the powers of gene editing, ...

AI could deliver substantially greater efficiencies in cell and gene therapy manufacturing and enable more patients to ...

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...

Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease, the ...

NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...