Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...
The gene-editing treatment will be available to certain patients with sickle cell disease in England as Vertex commits to collecting additional data.
Gene therapy using modified blood stem cells helped five adults with severe hemophilia A reach therapeutic levels of clotting ...
NHS officials estimate around 50 people a year will receive treatment now it has been approved for use for certain patients with severe sickle cell disease. | ITV National News ...
Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...
The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...
January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...
NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...
Department of Gastroenterology, Beijing Friendship Hospital, Capital Medical University, State Key Laboratory for Digestive Health, National Clinical Research Center for Digestive Disease, Beijing ...
The UK has approximately 17,500 individuals living with sickle cell disease, a condition particularly prevalent amongst those ...
By modifying 20 regions of the genome, scientists successfully bred mice with two male parents and raised them to maturity.