The prospects for a one-time treatment that reduces the risk of heart disease for the rest of a person’s life just got ...

Additionally, improving CAR-T biological efficiency could reduce dosing needs, further cutting costs and expanding access.

When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

Multidisciplinary coordination across prescribing teams, nursing, laboratory medicine, finance, and infusion centers is crucial for gene therapy delivery in Duchenne muscular dystrophy (DMD).

The FDA granted regenerative medicine advanced therapy designation to ATSN-201, a gene therapy candidate for the treatment of ...

Gene therapy for cystic fibrosis is advancing fast. Explore key biotech players, clinical progress, and its potential to ...

A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular ...

Scientists at the University of California, Riverside, have discovered how adult stem cells retain their regenerative power.

Verve Therapeutics said Monday that initial data show that its investigational gene-editing therapy lowered cholesterol ...

Gene therapy, with its offer of a possible cure for rare diseases like sickle cell, is losing early investors to higher-reward sectors like obesity and cancer, as sales for some of the new treatments ...

A team at the Centro Nacional de Investigaciones Cardiovasculares (CNIC) has developed an innovative gene-therapy strategy ...

Investigators have developed STITCHR, a new gene editing tool that can insert therapeutic genes into specific locations without causing unwanted mutations. The system can be formulated completely as ...