The prospects for a one-time treatment that reduces the risk of heart disease for the rest of a person’s life just got ...

Additionally, improving CAR-T biological efficiency could reduce dosing needs, further cutting costs and expanding access.

When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

Multidisciplinary coordination across prescribing teams, nursing, laboratory medicine, finance, and infusion centers is crucial for gene therapy delivery in Duchenne muscular dystrophy (DMD).

The FDA granted regenerative medicine advanced therapy designation to ATSN-201, a gene therapy candidate for the treatment of ...

A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective treatments.

Scientists at the University of California, Riverside, have discovered how adult stem cells retain their regenerative power.

Verve Therapeutics said Monday that initial data show that its investigational gene-editing therapy lowered cholesterol ...

Droplet digital PCR measurements of circulating tumor (ct)DNA to assess minimal residual disease before the initiation of ...

Monitoring blood levels of DNA fragments shed by dying tumor cells may accurately predict skin cancer recurrence, a new study ...

Feb. 7, 2025 — A research team has made a major discovery on how the CUL5 gene affects CAR-T cell therapy, an advanced cancer therapy. The study reveals that reducing the activity of the CUL5 ...