Nothing could've prepared columnist Helen Baldwin for her late son Jeffrey's diagnosis of SMA type 1 in the late 1990s.

Liver damage related to Zolgensma gene therapy usually resolves within a few months of treatment, a study found.

Connie Chandler is the director of family engagement at the nonprofit organization We Carry Kevan. She grew up in the ...

Connie Chandler is a columnist for BioNews and the Director of Family Engagement at the nonprofit organization, We Carry Kevan. She grew up in the foothills of North Carolina but now owns a home and ...

In her debut column of "Caring Together," Connie Chandler reflects on her college days, when friends volunteered to help with ...

For a boy with SMA in China, starting Evrysdi (risdiplam) just 12 days after birth was safe and helped him reach key motor ...

Researchers studied 118 SMA type 2 patients and saw their RULM scores stayed higher than expected had their disease kept its ...

Drawing on some previous volunteer experience, columnist Sherry Toh takes on a new role at SMA News Today: forum moderator.

DySMA, to assess swallowing in children with SMA while undergoing treatment, was applied to healthy children to facilitate comparisons.