Panelists discuss how spinal muscular atrophy (SMA) treatment will evolve over the next 5 years, likely incorporating ...

In a Phase I study, previously treated pediatric SMA patients exhibited reductions in a marker of neurodegeneration after salanersen treatment.

Children with infantile-onset Pompe's disease experienced motor function and cardiac improvements after receiving an ...

Jaipur: The life of 20-month-old Kartik hangs in balance. Diagnosed with spinal muscular atrophy (SMA), a rare and life-threatening neuromuscular dise.

Panelists discuss how insurance challenges impact spinal muscular atrophy (SMA) care, with prior authorizations becoming more ...

5q-Spinal muscular atrophy (SMA) is a progressive, autosomal recessive neuromuscular disease with an incidence of 1 in 14,848 births.1 SMA is characterised by proximal muscle weakness and in severe ...

Improving sleep quality with SMA can involve support for physical comfort, breathing, muscle weakness, and body temperature.

BASEL, Switzerland I June 15, 2025 I Roche (SIX: RO, ROG; OTCQX: RHHBY) announced today new dosing restrictions, effective immediately, for ELEVIDYS™ ...

Speech therapy helps people with SMA by improving speech clarity, breath control, swallowing, and communication device use.

Emerging Spinal Muscular Atrophy therapies in the different phases of clinical trials are- SKG 0201, Spinal muscular atrophy gene therapy, BIIB115, GC101, EXG001-307, Apitegromab, Talditercept ...