Living with SMA isn't just about survival, says columnist. There's also the emotional weight of preparing for the next crisis ...

Panelists discuss how spinal muscular atrophy (SMA) treatment will evolve over the next 5 years, likely incorporating ...

In a Phase I study, previously treated pediatric SMA patients exhibited reductions in a marker of neurodegeneration after salanersen treatment.

Children with infantile-onset Pompe's disease experienced motor function and cardiac improvements after receiving an ...

Jaipur: The life of 20-month-old Kartik hangs in balance. Diagnosed with spinal muscular atrophy (SMA), a rare and life-threatening neuromuscular dise.