A Northeast Ohio woman and a 22-year-old man from UAE are among the first patients to receive the innovative CRISPR treatment ...

Repositioning genes awakens fetal hemoglobin to treat disease. CRISPR editing may change future gene therapy. Researchers ...

Dr. Omar Llaguna, specialist in surgical oncology, programs a HistoSonics medical device for targeting a medium that mimics a liver tumor in a human body to demonstrate how a histotripsy procedure ...

Vertex Pharmaceuticals may have narrowed its focus this year, but the biopharma’s decision to stick with its remaining islet ...

Post-birth diagnosis resulting in early treatment can substantially improve the quality of life and reduce mortality in ...

Vertex Pharmaceuticals locked arms with Ono Pharmaceutical in an exclusive deal to advance povetacicept, targeting B ...

Penn researchers believe new potential gene therapy for glioblastoma brain cancer offers ‘a lot of hope’ Glioblastoma has been deadly and hard to treat, but researchers say they’ve made progress with ...

Discover what clinical trials are, why they're vital for new treatments, and how you can participate in life-changing medical ...