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A St George couple is asking the community after their three-year-old daughter was diagnosed with a rare genetic condition.
Today, we are highlighting a rare genetic disorder. Morquio syndrome challenges families and scientists worldwide. New advances in research spark hope for those living ...
In 2015, NICE said that BioMarin's Vimizim could be used to treat patients with the ultra-rare disease Morquio A syndrome, while real-world data was collected on its efficacy. Now – almost seven ...
Olivia Vitello, 14, spoke to the crowded room about her rare genetic disorder, called MPS Type A or Morquio Syndrome, and how she's received help from Seattle Children's Hospital since she was ...