Only five days after FDA approval of Yutrepia, Liquidia announced its first commercial shipment of the therapy, making prescriptions available to patients at specialty pharmacies. “We have moved with ...

Researchers have developed a gene therapy that significantly slowed motor function loss in preclinical models of amyotrophic ...

In May 2025, researchers announced that K.J. Muldoon, a baby boy born without the ability to process dietary protein properly ...

Last month, a baby got the world’s first personalized gene-editing treatment. What will this mean for millions of others with ...

Use precise geolocation data and actively scan device characteristics for identification. This is done to store and access ...