CDMO Rentschler Biopharma is signalling its intent to cut down cell and gene therapy operations by shutting down its UK manufacturing facility in Stevenage.

The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...

The gene-editing treatment will be available to certain patients with sickle cell disease in England as Vertex commits to collecting additional data.

Billie Eilish and Green Day kicked off the FireAid benefit concert in Los Angeles on Thursday night - a two-venue, five-hour ...

President Trump signed an executive order on the day of his inauguration that created doubts about the future of a program to ...

REGENXBIO is a longtime player in the gene therapy space, but one that’s yet to bring its own therapy to market (in the early ...

Fractyl Health is deprioritizing a type 2 diabetes trial in favor of a pivotal study of its endoscopy treatment Revita and ...

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...

Vertex Pharmaceuticals (VRTX) stock gains as England opts to reimburse its CRSPR (CRSP)-partnered gene therapy Casgevy to ...

BOISE — Sen. Brandon Shippy, R-New Plymouth, is proposing to put a 10-year pause on certain types of vaccines that were used ...

The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...