The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...

CDMO Rentschler Biopharma is signalling its intent to cut down cell and gene therapy operations by shutting down its UK manufacturing facility in Stevenage.

President Trump signed an executive order on the day of his inauguration that created doubts about the future of a program to ...

AI could deliver substantially greater efficiencies in cell and gene therapy manufacturing and enable more patients to ...

Since two groundbreaking treatments were approved in late 2023, only a handful of patients have been able to access the ...

For recurrent respiratory papillomatosis (RRP), novel gene therapy to jump-start immunity to the human papillomavirus (HPV) ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and ...

People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...

Despite mixed results using gene therapies to treat Duchenne muscular dystrophy, drug developers are pushing ahead with the ...

Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease, the ...

Taysha Gene Therapies offers hope for Rett syndrome with innovative treatment, strong trial results, and promising regulatory ...