A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

The UK has approximately 17,500 individuals living with sickle cell disease, a condition particularly prevalent amongst those ...

NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...

Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.

Despite mixed results using gene therapies to treat Duchenne muscular dystrophy, drug developers are pushing ahead with the ...

NHS officials estimate that around 50 people a year will receive treatment now that it has been approved for use for certain ...

South San Francisco, CA, January 30, 2025 – The California Institute for Regenerative Medicine (CIRM), one of the world’s largest institutions dedicated to regenerative medicine, has awarded nearly ...

Everything you need to know about agonising sickle cell disease and the ‘revolutionary’ new DNA therapy that's being rolled ...

A £1.65 million treatment has been approved for use for some NHS patients, offering hope of a cure to those with an inherited ...

Global biopharmaceutical manufacturing firm Rentschler Biopharma will shutter its United Kingdom facility as the ...