A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

A £1.65 million treatment has been approved for use for some NHS patients, offering hope of a cure to those with an inherited ...

The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...

Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...

Florida Cancer Specialists & Research Institute, LLC (FCS) this week celebrated the opening of a new state-of-the-art ...

Vertex Pharma has secured FDA approval for its non-opioid pain drug suzetrigine, becoming the first new class of pain ...

Australian researchers have successfully introduced an improved version of Cas12a gene-editing enzyme in mice.

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...

The company will use the funding to advance clinical trials for Tune-401, the epigenetic silencing drug for treating chronic ...

Gene therapy using modified blood stem cells helped five adults with severe hemophilia A reach therapeutic levels of clotting ...

The most complex engineering of human cell lines ever has been achieved by scientists, revealing that our genomes are more resilient to significant structural changes than was previously thought.