News

The prospects for a one-time treatment that reduces the risk of heart disease for the rest of a person’s life just got ...
The Food and Drug Administration (FDA) has granted Fast Track designation to PBGENE-HBV, an investigational gene editing therapy for adults with chronic hepatitis B.
The Boston-based company said its gene-editing treatment for people with high cholesterol was well-tolerated with no serious ...
Recently approved gene therapies offer patients one-time, potentially curative treatments for genetic diseases such as sickle ...
Investigators have developed STITCHR, a new gene editing tool that can insert therapeutic genes into specific locations without causing unwanted mutations. The system can be formulated completely as ...
Wall Street analysts said the results for Verve’s therapy appeared competitive on efficacy, while avoiding any major safety ...
Verve Therapeutics said Monday that initial data show that its investigational gene-editing therapy lowered cholesterol without inducing serious side effects.
Using gene editing with CRISPR-Cas9, the team has been able to study these proteins without altering ... Dec. 13, 2024 — Microorganisms produce a wide variety of natural products that can be ...
CRISPR-Cas9 gene editing technology has emerged as one of the most transformative advancements in medicine and biotechnology.
CRISPR-Cas9 genome editing exploits the CRISPR-Cas system to ... survival and for terminal erythroid differentiation. Gene-edited mouse models are crucial for disease research but remain ...
Along this line, two new types of gene editing has been developed to produce precise changes in genes: base editing, which can change a single DNA letter, and prime editing, which is able to delete or ...