The following is a summary of “Cutaneous manifestations of Fabry disease: A systematic review,” published in the March 2025 ...

"Health being a state subject, the primary responsibility of providing healthcare services is that of state governments.

Around 1,000 patients with rare diseases are registered with Centres of Excellence in India. The government allocated ...

Learn more about whether Alvotech or Amicus Therapeutics, Inc. is a better investment based on AAII's A+ Investor grades, ...

Idorsia Ltd (SIX: IDIA) today announced the publication of the Annual Report 2024 - consisting of the Business Report, ...

We also support scientific advancement through targeted grant programmes, such as findforrare.com, to ensure ongoing research in Fabry disease, alpha‐mannosidosis, and nephropathic cystinosis.

For example, at the SSIEM Annual Symposium earlier this month, the company shared data on a new candidate for the treatment of Fabry disease, a rare genetic blood disorder. Chiesi’s approach to ...

Ad hoc announcement pursuant to Art. 53 LR Allschwil, Switzerland - March 27, 2025Idorsia Ltd (SIX: IDIA) today announced the publication of the Annual Report 2024 - consisting of the Business Report ...

It also develops 4D-175 for geographic atrophy in preclinical with open IND; 4D-725 for alpha-1 anti-trypsin deficiency lung disease in preclinical; and 4D-310 for Fabry disease, which is in Phase ...

Quadriparesis is when there is muscle weakness in both arms and both legs. It is different than quadriplegia, which causes paralysis (complete loss of movement) in each of the body’s limbs. The ...

Reduced activity of these enzymes may indicate the diseases mucopolysaccharidosis type I (MPS-1), Pompe, Gaucher or Fabry, respectively. These four diseases occur in about one of every 1,500 to ...