Crispr Therapeutics is an emerging gene editing company focused on the development of Crispr/Cas9-based therapeutics. The company's proprietary platform specializes in clustered regularly interspaced ...

A Tennessee family has opened up about their young daughter's devastating battle with a rare disorder that has caused her to ...

Regular physical activity, such as dance or targeted exercise, can slow the progression of Parkinson’s disease, helping ...

Discover why BTK inhibitors have attracted interest for treating multiple sclerosis, as a few late-stage candidates close in ...

It was a packed house at Yee-Haw Brewing in North Knoxville as hundreds gathered to show their support for the Begbie family and others who have children with Sanfilippo Syndrome.

An editorial published in Brain Medicine reveals that many widely prescribed medications may disrupt sterol biosynthesis—an essential process for brain development—potentially causing harm similar to ...

A preclinical study from scientists at Scripps Research finds that a drug already FDA-approved for treating inflammatory conditions may help reduce both alcohol intake and pain sensitivity-two issues ...

Researchers have developed engineered human microglia that detect disease-related brain changes and release therapeutic ...

NS-229 is an investigational selective Janus kinase 1 inhibitor designed to prevent tissue damage caused by EGPA by suppressing immune cell activation.