Xenon Pharmaceuticals is developing a drug for the most common type of seizure experienced by people with epilepsy. Here's ...

Her son Ben, she learned, had mucopolysaccharidosis (MPS) type 2, or Hunter Syndrome, one of a group of rare diseases that is ...

Thirty years after scientists demonstrated how brain implants can help rhesus monkeys move robotic limbs using only their ...

When Elise Felicione tried to design a clinical trial for a supplement, 5 things got in the way. It’s a lesson for the ...

The FDA’s recent rejection of a rare disease cell therapy — despite prior internal support and an approval in Europe — is prompting questions about whether the agency’s rhetoric matches its regulatory ...

An experimental therapy for a rare blood cancer was rejected by the FDA though internal reviewers had recommended it be cleared ...

Sarepta's CEO will retire after a tumultuous decade in which Sarepta became a $15 billion company — and then that value ...

Vice President JD Vance announced Wednesday that the Trump administration would “temporarily halt” some Medicaid funding to ...

Casey Means wanted to talk about chronic disease. But Bill Cassidy wanted to hear about her views on vaccines.

Paul Offit, a renowned vaccine inventor and former CDC adviser, has been asked three times to debate health secretary Robert F. Kennedy Jr., he said yesterday at a webinar hosted by MedPage Today.

Casey Means, now the epitome of a “MAHA mom," invokes motherhood and “wholeness” in health in making her case to be the U.S.

Debra Manetta is a writer and certified life coach in New Rochelle, N.Y., and the sibling of a brother who lived with schizophrenia. She also brings experience as a parent of a child with ...