The MPS disease most commonly seen in children is the adult form of chronic myelogenous leukemia (CML) (t[9:22] or BCR/ABL containing CML). This is the subject of a separate review and is not ...

Andrew Gwynne, who lost his parents to cancer, told the Commons tackling rarer types will be a ‘crucial part’ of the emerging ...

England’s chief medical officer Chris Whitty warned against rushing to meet ‘firm deadline’ for as he gave evidence to MPs ...

"RGX-121 and RGX-111 represent one-time gene therapies that can potentially change the course of MPS disease, and we are very pleased to be partnering with REGENXBIO, experts in gene therapy ...

In a letter to environment secretary Steve Reed, the cross-party group of 42 MPs and peers call for government backing for a ...

Farmers and bird keepers have been told to remain vigilant following an outbreak of bird flu, as MPs heard the virus is the ...

The UK took a week to prevent meat and other animal products entering the country from Germany last month, despite German ...

Nippon Shinyaku to lead commercialization of first potential gene therapies for Mucopolysaccharidosis II (MPS II) and Mucopolysaccharidosis I (MPS I) in U.S. and Asia REGENXBIO retains rights to ...

RGX-121 is poised to be the first gene therapy for MPS II with potential FDA approval as early as late 2025, and RGX-111 has demonstrated very promising results in Phase 1/2 study. With Nippon ...