In the US, Hemgenix is priced at $3.5 million – making it the most expensive medicine in the world – and above the $2.9 million that the influential Institute for Clinical and Economic Review ...

The withdrawal of fidanacogene elaparvovec leaves one gene therapy-- etranacogene dezaparvovec (Hemgenix) -- approved for ...

uniQure and CSL have become the first pharma companies to get regulatory approval for a gene therapy for haemophilia B anywhere in the world, after the FDA cleared their Hemgenix therapy for ...

at the Comprehensive Care Center of the University Hospital of Medicine Vienna. HEMGENIX ® is the first one-time gene therapy approved in Europe for the treatment of adults with severe and moderately ...