The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...

President Trump signed an executive order on the day of his inauguration that created doubts about the future of a program to ...

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...

People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and ...

AI could deliver substantially greater efficiencies in cell and gene therapy manufacturing and enable more patients to ...

This new tool, known as minimal, versatile genetic perturbation technology (mvGPT), combines the powers of gene editing, ...

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

The bill would implement a moratorium for a decade. “I am not against vaccination in any way,” the freshman lawmaker said.

Taysha Gene Therapies offers hope for Rett syndrome with innovative treatment, strong trial results, and promising regulatory ...

Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease, the ...