The University of Southern California (USC) has received a $6m grant from the California Institute for Regenerative Medicine ...

The California Institute for Regenerative Medicine has awarded a $6 million grant to USC investigators pioneering a new first ...

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...

For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that ...

A personalised vaccine for the aggressive and fatal brain cancer glioblastoma has shown encouraging ... a spin-out from the university. Vertex's gene-editing therapy for sickle cell disease ...

The term MGMT-unmethylated glioblastoma refers to a genetic alteration of the brain cancer where the MGMT gene is not methylated ... RNA [mRNA] backbone therapy. The ability to achieve both ...

Brain cancer is the second-leading cause of death in children in the developed world. For the children who survive, standard ...

A detailed analysis of brain cell gene expression over time revealed the genetic origins of autism and glioblastoma at young ages. Image by Li Wang and Songcang Chen/Kriegstein Laboratory UCSF ...

International collaborations, refined gene-editing protocols, and targeted immunologic maneuvers keep the cancer gene therapy ...