The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

President Trump signed an executive order on the day of his inauguration that created doubts about the future of a program to ...

Despite mixed results using gene therapies to treat Duchenne muscular dystrophy, drug developers are pushing ahead with the ...

The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...

People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...

AI could deliver substantially greater efficiencies in cell and gene therapy manufacturing and enable more patients to ...

The bill would implement a moratorium for a decade. “I am not against vaccination in any way,” the freshman lawmaker said.

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and ...

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...

Taysha Gene Therapies offers hope for Rett syndrome with innovative treatment, strong trial results, and promising regulatory ...

Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease, the ...

NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...