CHICAGO – A CRISPR-Cas9-based investigational therapy was linked with a drop in serum transthyretin (TTR) levels in patients with transthyretin amyloidosis with cardiomyopathy (ATTR-CM ...

When targeting these cancers in mice, a single treatment with the novel CRISPR system doubled the survival ... The molecular scissors of Cas9 cut the cancer cell’s DNA, thereby neutralizing ...

This study presents an optimized CRISPR-Cas12a system for large-scale genetic screening, revealing critical genes involved in lymphoma development and therapy.

Akribion Therapeutics emerges from stealth with €8 million in seed funding to develop a novel cancer RNA-guided approach ...

Why are CRISPR companies not OK? Will Robert F. Kennedy Jr. keep his promises if he's confirmed to lead the Department of ...

Researchers using CRISPR-Cas9 gene editing tools have discovered that while this ... including high-throughput libraries for studying cancer genetics and novel systems for tracking gene expression in ...

Potent in vivo gene editing in skeletal muscle of non-human primates by a novel, ultracompact CRISPR system delivered via a single AAV vector.

By creating gene editors not found in nature, or optimizing existing editors, AI can improve the accuracy, effectiveness, and accessibility of gene editing.

In his lab, Gonzalez-Fernandez integrates cutting-edge technologies such as CRISPR/Cas9, 3D printing, and novel bioinks to explore applications like in situ gene editing for tissue repair ...

A first patient has been treated in a trial of an Allergan and Editas drug based on CRISPR/Cas9, a technology that allows genes to be manipulated inside the body. The two companies claim AGN ...