Achondroplasia is a type of dwarfism that affects the growth in children, leading to a short stature or small size. Achondroplasia is a rare genetic condition that affects one in every 15,000 to ...

Children of all ages with achondroplasia are now included in ... a professor of human genetics at Emory University, said in a statement. 1 “I am delighted that [vosoritide] is now approved ...

In this phase 2 dose-finding study, we evaluated the safety and efficacy of oral infigratinib in children with achondroplasia between the ages of 3 and 11 years. A total of 72 children were ...

New Data Highlights VOXZOGO Long-Term Efficacy, Safety and Quality of Life in Achondroplasia 7-year Phase 2 Results in Achondroplasia Data from two studies of VOXZOGO in children ≥5 years of age ...

Achondroplasia, the most common form of skeletal ... data to be presented at the 2024 American College of Medical Genetics and Genomics Annual Clinical Genetics Meeting, including the six poster ...